CRISPR genome-editing grows up: advanced therapies head for the clinic
Gene-editing therapies like Casgevy show long-lasting benefits for blood disorders but face challenges in accessibility due to complexity and cost.
The First Crispr Treatment Is Making Its Way to Patients
The first CRISPR-based treatment, Casgevy, has been approved for sickle cell disease and beta thalassemia, marking a significant advance in gene-editing therapies.
CRISPR genome-editing grows up: advanced therapies head for the clinic
Gene-editing therapies like Casgevy show long-lasting benefits for blood disorders but face challenges in accessibility due to complexity and cost.
The First Crispr Treatment Is Making Its Way to Patients
The first CRISPR-based treatment, Casgevy, has been approved for sickle cell disease and beta thalassemia, marking a significant advance in gene-editing therapies.
FDA approves first CRISPR therapy-here's how it works against sickle cell
The FDA has approved two gene therapies for the treatment of sickle cell disease, one of which is the first CRISPR/Cas9-based treatment to be approved in the US.
Sickle cell disease affects around 100,000 people in the US and can lead to anemia, organ damage, and early death.
Sickle cell gene therapies roll out slowly
FDA has approved the first genetic treatments for sickle cell disease, offering new hope to patients like Olaide Adekanbi.
Doctors cured her sickle-cell disease. So why is she still in pain?
Genesis Jones underwent a stem cell transplant to cure her sickle-cell disease, but continues to face significant health challenges and isolation post-treatment.
New Sickle Cell Treatments Reach Patients after Years of Effort
Sickle cell disease is complicated, affecting treatment despite a single genetic cause.
Research is multifaceted, targeting multiple levels to address the disease's complexity.
First Sickle Cell Gene Therapy Patient, 12, Leaves Hospital
Kendric Cromer received the first gene therapy for sickle cell disease, representing a significant breakthrough in treatment.
What Is Sickle Cell Disease?
Sickle cell disease is caused by a point mutation in the HBB gene that impacts hemoglobin function and structure.
FDA approves first CRISPR therapy-here's how it works against sickle cell
The FDA has approved two gene therapies for the treatment of sickle cell disease, one of which is the first CRISPR/Cas9-based treatment to be approved in the US.
Sickle cell disease affects around 100,000 people in the US and can lead to anemia, organ damage, and early death.
Sickle cell gene therapies roll out slowly
FDA has approved the first genetic treatments for sickle cell disease, offering new hope to patients like Olaide Adekanbi.
Doctors cured her sickle-cell disease. So why is she still in pain?
Genesis Jones underwent a stem cell transplant to cure her sickle-cell disease, but continues to face significant health challenges and isolation post-treatment.
New Sickle Cell Treatments Reach Patients after Years of Effort
Sickle cell disease is complicated, affecting treatment despite a single genetic cause.
Research is multifaceted, targeting multiple levels to address the disease's complexity.
First Sickle Cell Gene Therapy Patient, 12, Leaves Hospital
Kendric Cromer received the first gene therapy for sickle cell disease, representing a significant breakthrough in treatment.
What Is Sickle Cell Disease?
Sickle cell disease is caused by a point mutation in the HBB gene that impacts hemoglobin function and structure.
The U.S. FDA has approved the first gene therapy treatment based on CRISPR technology.
The treatment, called exa-cel, is approved for sickle cell disease and may also be approved for beta thalassemia.
FDA approves first CRISPR gene editing treatment that may cure sickle cell disease
Regulators have approved two new gene therapies for sickle cell disease that could potentially cure the inherited blood disorder.
The treatments are the first to be approved based on CRISPR, the gene editing tool that won its inventors the Nobel Prize in 2020.
FDA approves CRISPR-based therapy for sickle cell disease
The FDA has approved the first therapy using CRISPR gene-editing technology to treat sickle cell disease.
The technology has the potential to be applied to other blood disorders, certain cancers, and infectious diseases.
Breakthrough Gene Treatments For Sickle Cell Disease Approved
Regulators have approved two new gene therapies for sickle cell disease, offering hope for a cure for the painful blood disorder
The treatments are designed for patients 12 and older with severe forms of the disease, and one of them is the first therapy based on CRISPR gene editing
FDA approves first gene-editing treatments for human illness
The FDA has approved the first gene-editing treatments for sickle cell disease, marking a milestone in the field of gene-editing.
The treatments have the potential to provide more targeted and effective treatments for rare diseases with limited current options.
F.D.A. Approves Sickle Cell Treatments, Including One That Uses CRISPR
The Food and Drug Administration has approved the first gene editing therapy and conventional gene therapy for sickle cell disease.
Obstacles to treatment include limited access to authorized medical centers, individualized procedures, and high costs.
Possible Therapy for Sickle Cell Won't Cure Its Racist Legacy - Non Profit News | Nonprofit Quarterly
The FDA is reviewing an experimental gene therapy treatment for sickle cell disease.
Racism has significantly affected the healthcare and outcomes of sickle cell disease patients.
The CRISPR Era Is Here
Gene-editing technology CRISPR has successfully treated a patient with sickle-cell disease, providing hope for future treatments.
The treatment resulted in the patient living virtually symptom-free, with 29 out of 30 eligible patients experiencing zero pain crises after treatment.